Beta Thalassemia: Practice Essentials, Etiology, Epidemiology
Β-Thalassemias | NEJM
Thalassaemia - The Lancet
Current and future alternative therapies for beta-thalassemia major - ScienceDirect
2021 update on clinical trials in β‐thalassemia - Musallam - 2021 - American Journal of Hematology - Wiley Online Library
JCM | Free Full-Text | Does Hepcidin Tuning Have a Role among Emerging Treatments for Thalassemia?
Antioxidants as Complementary Medication in Thalassemia | IntechOpen
Non-transfusion-dependent thalassemias | Haematologica
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Safety and efficacy of thalidomide in patients with transfusion-dependent β- thalassemia: a randomized clinical trial | Signal Transduction and Targeted Therapy
Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia
Replacing the suppressed hormone: toward a better treatment for iron overload in β-thalassemia major? | Haematologica
PDF) Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm
β-Thalassemia | Genetics in Medicine
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
Gene Therapy For Beta-Thalassemia: Updated Perspectives | TACG
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Full article: Revisiting beta thalassemia intermedia: past, present, and future prospects
Β-Thalassemias | NEJM
Sirolimus for Treatment of β-Thalassemia: From Pre-Clinical Studies to the Design of Clinical Trials
Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary Myelofibrosis
Significance of genetic modifiers of hemoglobinopathies leading towards precision medicine | Scientific Reports
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
Cureus | Improving Ineffective Erythropoiesis in Thalassemia: A Hope on the Horizon
IJMS | Free Full-Text | Non-Transfusion-Dependent Thalassemia: An Update on Complications and Management
Pathophysiology and treatment of patients with... | F1000Research
A paradigm shift on beta-thalassaemia treatment: How will we manage this old disease with new therapies? - ScienceDirect
